How We Fight

Researchers Talk About FightSMA from FightSMA on Vimeo.

FightSMA engages leading scientists and policymakers to pursue a cure for spinal muscular atrophy. For nearly 25 years, FightSMA has pioneered efforts in four major areas:  

Advancing Science

FightSMA invests in a broad range of promising research efforts, critically reviewing the full spectrum of science and possibility until an effective cure is found.  Click here to learn about 25 years of FightSMA-funded research.

Advocating for Policy

FightSMA engages government leaders and policy makers globally to build support for pediatric research.

Raising Awareness

FightSMA actively shapes the global dialogue concerning sma research and advancements.

Equipping Families

FightSMA equips and empowers families to fight back and find answers.


"FightSMA has been a pioneer in funding labs that identify novel, so-called, smn2 inducers — called by a variety of names. This work has really been important in identifying novel classes of potential SMA therapies."

Dr. Alex E. Mackenzie

Professor, Pediatrics and Biochemistry,
University of Ottawa Director,
Children's Hospital of Eastern Ontario Research Institute

Click here to read more quotes from researchers about FightSMA